ANPDFFeb 11 minResearchIntraBio Community Update | February 1, 2024New Drug Application for IB1001 for the treatment of NP-C disease was submitted to the US FDA in January 2024 Read the full statement...
ANPDFJan 91 minCommunityZevra Therapeutics Media Release | January 8, 2024Zevra Therapeutics Receives FDA Acceptance Of Resubmission Of NDA For Arimoclomol As A Treatment For Niemann-Pick Disease Type C Read the...
Ellie Van VelsenJan 83 minCommunityNP-C Corner: Will I be a lab rat? An exploration of clinical trials in the world of Niemann-Pick.Ellie explores what clinical trials are and how they impact patients of Niemann-Pick diseases.