The 2025 Australian Niemann-Pick Conference brought together families, clinicians, and researchers for two days of powerful connection, cutting-edge science, and shared lived experience. Highlights included the launch of Australia’s first NPC care standard, moving keynote talks, and vital updates on global clinical trials.

June 18, 2025 – Newark, NJ Rafael Holdings has announced that an independent Data Monitoring Committee (DMC) has completed its scheduled...