The ANPDF is a key contributor to the vital NP-C research conducted at The Florey Institute of Neuroscience and Mental Health.
Current research projects in the Oxidation Biology Unit at The Florey Institute of Neuroscience and Mental Health (Melbourne, Australia) are led by Dr. Ya Hui Hung and Professor Ashley Bush.
The Australian NPC Disease Foundation strongly supports this research to find new treatment options that will provide better health outcomes for NP-C patients both in Australia and around the world.
Their research currently focuses on screening drug candidates using NP-C patient cells. There is excellent progress in identifying drug candidates that can restore cholesterol processing, which may lead to new treatment options for NP-C.
Research Goals + Progress
The path to developing a new medicine is a long and expensive journey which the ANPDF is committed to traveling with The Florey.
It is estimated from Discovery to Clinical Trials to take 10+ years and USD 94 million.
With your support, the goal is to move into the second stage of this process within the next 12 months, bringing us one vital step closer to offering a local and life-changing treatment to Aussies suffering from Niemann-Pick disease type C.
Meet the Research Team
Prof. Mark Walterfang
Neuropsychiatrist consultant and senior staff specialist at the Neuropsychiatry Unit, Royal Melbourne Hospital (Australia); an honorary clinical Professor at the Department of Psychiatry, University of Melbourne (Australia) and The Florey.