Research Updates

Azafaros Media Release | July 16, 2024

Azafaros announces positive topline Phase 2 study data with nizubaglustat in GM2 gangliosidosis and Niemann-Pick disease type C Read the...

Intrabio Media Release | June 29, 2023

"IntraBio Announces Positive Pivotal Trial Results of IB1001 for the Treatment of Niemann-Pick Disease Type C" Read the full article...

It's a wrap! 2022 NPC Conference

The annual NPC Conference, both live and online, attended by patients, families, clinicians and researchers of Niemann-Pick disease.

Niemann-Pick Disease Type C: Working together to make a difference

This lecture will present the Australian collaboration and latest research on NP-C, a rare genetic disorder that leads to childhood...

Reconnecting at the 2021 NPC Conference

Adapting to the times, our Australian NPC community had the opportunity to connect at this year's conference with our first-ever...