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Community News and Events

Welcome to the ANPDF blog, where we share the latest updates, stories, and breakthroughs in the fight against Niemann-Pick Disease. Join us as we raise awareness, support families, and drive research forward.

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Zevra Therapeutics Media Release | November 20, 2023

Zevra announces the completion of its acquisition of Acer Therapeutics. Zevra states they are committed to the arimoclomol expanded...

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Nov 21, 20231 min read

Kisbee Therapeutics and Zevra Therapeutics Updates

"We remain steadfast in our key priorities to the NPC community," - Zevra Therapeutics Read the full statement from Zevra Therapeutics...

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Sep 11, 20231 min read

Azafaros Media Releases | January 5-9, 2023

"Azafaros Receives FDA's IND Clearance and Fast Track Designation for Lead Asset AZ-3102" Read the press release from January 5, 2023...

ANPDF

Jan 10, 20231 min read

Intrabio Media Release | December 5, 2022

"IntraBio Ltd. is pleased to confirm that it has completed recruitment for its Pivotal Trial, Effects of N-Acetyl-L-Leucine on...

ANPDF

Dec 6, 20221 min read

Pfrieger's Digest | Issue 7 - September 2022

Pfrieger's Digest for Niemann-Pick type C: Summaries of research advances on selected peer-reviewed publications in scientific journals....

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Oct 10, 20221 min read

It's a wrap! 2022 NPC Conference

The annual NPC Conference, both live and online, attended by patients, families, clinicians and researchers of Niemann-Pick disease.

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Jun 30, 20222 min read

Pfrieger's Digest | Issue 6 - May 2022

Pfrieger's Digest for Niemann-Pick type C: Summaries of research advances on selected peer-reviewed publications in scientific journals....

ANPDF

Jun 6, 20221 min read

New Research Study for Childhood Dementia

Dementia-CONNECT: Connecting the dots in Childhood Dementia disorders Researchers at The Sydney Children’s Hospital Network (SCHN) are...

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Apr 28, 20222 min read

New Research Article | January 26, 2022

New research article published: "Severely impaired CTL killing is a feature of the neurological disorder Niemann-Pick Syndrome type C1"

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Jan 29, 20221 min read

Niemann-Pick Disease Type C: Working together to make a difference

This lecture will present the Australian collaboration and latest research on NP-C, a rare genetic disorder that leads to childhood...

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Oct 10, 20211 min read

Reconnecting at the 2021 NPC Conference

Adapting to the times, our Australian NPC community had the opportunity to connect at this year's conference with our first-ever...

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Jul 27, 20211 min read

A New Tradition: NP-C Scientific Symposium and Family Conference

Providing an opportunity for both Australian and International professionals to collaborate on all aspects of Niemann-Pick type C...

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Jul 20, 20192 min read

Community News and Events

Topics

Zevra Therapeutics Media Release | November 20, 2023

Kisbee Therapeutics and Zevra Therapeutics Updates

Azafaros Media Releases | January 5-9, 2023

Intrabio Media Release | December 5, 2022

Pfrieger's Digest | Issue 7 - September 2022

It's a wrap! 2022 NPC Conference

Pfrieger's Digest | Issue 6 - May 2022

New Research Study for Childhood Dementia

New Research Article | January 26, 2022

Niemann-Pick Disease Type C: Working together to make a difference

Reconnecting at the 2021 NPC Conference

A New Tradition: NP-C Scientific Symposium and Family Conference