ANPDFMar 25, 20221 minResearchAzafaros Media Release | March 24, 2022"Second Orphan Drug Designation Supports Azafaros’ Strategy to Develop AZ-3102 as a Disease Modifying Treatment in a Range of Severe Rare...
ANPDFMar 25, 20221 minResearchOrphazyme Media Release | March 22, 2022"Orphazyme announces withdrawal of European Marketing Authorisation Application for arimoclomol for the treatment of Niemann-Pick disease...
ANPDFMar 7, 20222 minEvents2022 NPC Charity Gala Raised $275,000The second NPC Charity Gala was held February 26, 2022 - close to 2 years after the original date in Oct 2020. It was a great success,...